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    Related websites

    Official Patient Site | SPINRAZA® (nusinersen)

    WEBLearn about spinraza, a prescription medicine used to treat pediatric and adult patients with Spinal Muscular Atrophy (SMA). See Safety and Prescribing info. Visit Healthcare Professional Site

    Spinraza.com


    Nusinersen - Wikipedia

    WEBNusinersen, marketed as spinraza, is a medication used in treating spinal muscular atrophy (SMA), a rare neuromuscular disorder. In December 2016, it became the first approved drug used in treating this disorder.

    En.wikipedia.org


    Spinraza: Uses, Dosage, Side Effects, Warnings - Drugs.com

    WEBApr 4, 2023 · spinraza is used to treat spinal muscular atrophy (SMA), a decline in muscle strength over time, in adults and children. People with SMA have a mutated SMN1 gene and can’t generate enough SMN protein needed for …

    Drugs.com


    What is SMA? | SPINRAZA® (nusinersen)

    WEBSpinal Muscular Atrophy (SMA) is a disease of the central nervous system. Find info on what causes SMA, testing & treatment. See Safety & Prescribing Info.

    Spinraza.com


    Spinraza: Cost, How It’s Given, Use for SMA, Dosage, and More

    WEBAug 18, 2022 · Learn about cost, use, dosage, and more for spinraza (nusinersen), which is a prescription drug that treats spinal muscular atrophy in adults and children.

    Healthline.com


    How SPINRAZA® (nusinersen) Works

    WEBLearn how a spinraza injection effectively treats an underlying cause of SMA for those with Types 1, 2, and 3. See Safety & Prescribing Info.

    Spinraza.com


    Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA)

    WEBNusinersen, marketed in the U.S. as spinraza ® (Biogen) is the first therapy approved for the treatment of SMA. SMA results from mutations in a gene known as SMN1 , which encodes a protein (Survival Motor Neuron, or SMN) important for motor neuron survival.

    Ninds.nih.gov


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